| 2021 | Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study | Adams, David; Polydefkis, Michael; González-Duarte, Alejandra; Wixner, Jonas; Kristen, Arnt V.; Schmidt, Hartmut H.; Berk, John L.; Losada López, Inés Asunción; Dispenzieri, Angela; Quan, Dianna; Conceição, Isabel M.; Kyriakides, Theodoros; Waucquier, Nawal; Campana-Salort, Emmanuelle; Wiesman, Janice; Zueiter, Andreas; Rezk, Tamer; Perez, Javier M.; Castro, Isabel; Cardoso, Marcio; Ryder, Julie; Théaudin-Saliou, Marie; Zamba-Papanicolaou, Eleni; Kraus, Deborah; Kim, Byoung-Joon; Correia, Nuno; Min, Ju-Hong; Franco, Ana; Suhr, Ole; Katanazaka, Kimitaka; Taylor, Mark; Hayman, Suzanne R.; Agathangelou, Petros; Aldinc, Emre; Coskun, Derya J.; Diallo, Saran; Dias da Silva, Moises; Suan, Daniel; Dalton, James; Yang, Chih-Chao; Viera Lima, Ana Flavia; Mezei, Michelle M.; Brice, Sylvie; Sellers, Peter; Abu-Manneh, Rana; Cortese, Andrea; Leonidou, Eleni; Stone, Paula; Hobbs, Miriam; Cauquil-Michon, Cécile; Ehinger, Vincent; Balaya-Gouraya, Line; Boyer, Leslie; Seok, Jin Myoung; Signate, Aissatou; Khoshnoodi, Mohammad; Criollo Mora, Elia; Jozefowicz, Elsa; Wajnsztajn, Fernanda; Taniguchi, Ikuko; Eliahou, Ludivine; Pouget, Jean; Oda, Junko; Soderberg, Karin; Le Corvoisier, Philippe; Nienhuis, Hans; Chaudhry, Vinay; Victory, Jennifer; Yamashita, Taro; Rezzan, Kus Jülide; Guerrero Sola, Antonio; Luigetti, Marco; Dalia, Samir; Ajroud-Driss, Senda Ajroud-Driss; Kenepp, Amanda; Bournane, Halima; Hwa, Lisa; Segawa, Akiko; Martins da Silva, Ana; Kapoor, Prashant; Liu, Qingfeng; Hokezu, Youichi; Gorevic, Peter; Pinto, Luiz Felipe; Palacios, Marta; Lambrianides, Sakis; Berthelot, Emeline; Karamursel, Sacit; Tugal Tutkun, Nuriye Ilknur; Kasprzyk, Emmanuelle; Elrezzi, Elise; Gonzalez, Leidy J.; Verschueren, Annie; Sweetser, Marianne T.; García Feijoo, Julián; Rosti, Vittorio; Lee, Kia; Choi, Kyomin; Anan, Intissar; Mihailovic, Natasa; Oshita, Tomohiko; Rajkumar, Vincent S.; Pedrosa-Domellöf, Fatima; Hipólito Reis, Antonio; Koujin, Yoko; Walter, Doreen; Hosokawa, Yuko; Meguig, Sayah; Vista, Geno; Lozza, Alessandro; Hachulla, Eric; Lee, Hye Lim; Gauvain, Clement; Yeh, Shin-Joe; Martin, Nathalie; Dioso, Holly; Chu, Hanh; Özdemir, Betül; Frenzel, Lukas F.; Pytel Cordoba, Vanesa; Cherneva, Zheyna; Chacko, Liza; Tran, Leyla; Munoz Beamud, Francisco; Attarian, Shahram; Elabed, Mongia; Marques Júnior, Wilson; Pester, Lars; Gertz, Morie A.; Lazzari, Victoria; Hein, Selina; Orellana, Lucas G.; Stewart, Graeme; Sacko, Niamey; Pérez-Castañeda, Sandra Lorena; Marques Coutinho, Barbara; Coelho, Teresa; Lopate, Glenn; Ruiz, Julie; Sakurada, Naonori; Do, Thi Hoa (Therese); Gervais de Santa Rosa, Renata; Tournev, Ivaylo; Serbest, Nail G.; Freitas, Monica; Rodas Marin, Lida Maria; Nordh, Erik; Dyck, Peter; Mazzeo, Anna; Lin, Yi; DeLong, Douglas; Ernande, Laura; Vervoitte, Laetitia; Chan, Soo Looi; Zibert, Andree; Meng, Ulrike; Lee, Ming-Jen; Shah, Syed Mahmood; Yamanishi, Yuki; Miyazawa, Chinatsu; Zhelyazkova-Glaveeva, Sashka; Fujita, Akemi; Hsieh, Sung-Tsang; Gerk, Olga; Lee, Ga Yeon; Dingli, David; Vuong, Thao; Russo, Massimo; Hrkman, Nicole; Matsumoto, Kazuhiko; Miller, Sarah; Nguyen, David; Smith, Ashley; Rigo Oliver, Elena; Moreira, Carolina Lavigne; Martinez-Naharro, Ana; Takahashi, Tetsuya; Berber, Erhan; Low, Soon Chai; Koto, Shusuke; Shimomura, Masahiro; Itoya, Amenze; Ulbricht, Hannah; Ferreira, Natalia; Go, Ronald; Jarrett, Raquel; Cho, Eun Bin; Pu, Helen; Florence, Julaine; Algalarrondo, Vincent; Bernardo, Daniela; Li, Steve; Oda, Tetsuya; Taylor, Lenka; Vest, John; Jehan Lacour, Nathalie; Zepeda, Karla A.; Rakotondratafika, Fetra; Ye, Jing; Scheid, Christof; Morino, Hiroyuki; Overcash, J. Scott; Lachmann, Helen J.; Campistol, Josep M.; Cantú Brito, Carlos Gerardo; White, Matthew T.; O'Riordan, William; Inamo, Jocelyn; Paras, Allan; Sarafov, Staiko; Lahme, Larissa; Casey, Patricia; Heintzman, Sarah; Pinto, Marcus Vinicius; Vinas, Maita; Stephant, Maeva; Giang, Lien; Lin, Kon-Ping; Leung, Nelson; Lopes, Ana; Bisogni, Giulia; Kim, Arreum; Obici, Laura; Cárdenas-Soto, Karla; Friebel, Frauke; Monte, Julia R.; Litcanov, Debora Cristina; Bulthuis-Kuiper, Janita; Cohen, Oliver; Gamez Martinez, Jose M; Fukase, Emi; Brannagan III, Thomas H.; Gillmore, Julian D.; Descals, Cristina; Dávila, Lucía Galán; Cisneros Barroso, Eugenia; Truong, Nghi; Uson, Mercedes; Gonsalves, Wilson; Jose Vega, Francisco; Charlin, Cyril; Moritaka, Taiga; Huesing-Kabar, Anna; Mason, Garnette; Pereira, Pedro; Castro, Jose; Masuda, Teruaki; Sommerville, R. Brian; Figuerola, Antoni; Lust, John A; Chao, Chi-Chao; Mauricio, Elizabeth A.; Tard, Celine; Holtick, Udo; Romano, Angela; Kim, JuHyeon; Carrillo, Esmeralda; aus dem Siepen, Fabian; Lee, Yi-Chung; Not, Adeline; Giardino, Elena; Becquemont, Laurent; Kumar, Shaji K.; Hernandez Reyes, Jose Pablo; Sankey, Alison; Jack, Kristin; Barroso, Fabio; LoRusso, Samantha; Gaouar, Amina; Baskin, Amber; Lamas, Filipa; Lautre, Andrea; Schilling, Matthias; Rodríguez Rodríguez, Adrián; Chamova, Teodora; Wang, Jing Jing; Pessoa, Bernardete; Misumi, Yohei; Guimaraes, Nadia; Ueno, Hiroki; Dixon, Stacy; Waters, Michael; Law, Steven; Weimer, Louis; Deplanque, Dominique; Noe-Schwenn, Simone; Dimberg, Elliot; Cakar, Arman; Russell, Stephen J.; Shin, Hyun Jin; Beaudonnet, Guillemette; Harada, Masaya; Burks, Kathleen L.; Dang, Lien; Blume, Brianna; Tsang, Steven; Oh, Jeeyoung; Delmont, Emilien; Nezu, Tomohisa; Ueda, Akihiko; Wells, Karen; Alves, Cristina; Nakahara, Keiichi; Yorita, Akiko; Ando, Rina; González Moreno, Juan; Di Paolantonio, Andrea; Kishida, Dai; Tsuruhisa, Seiko; Elitok, Ali; Migaud-Chervy, Maria-Claire; Witzig, Thomas E.; Cioroiu, Comana; Arrouasse, Raphaele; Perez de Isla, Leopoldo; Allen, Adriane C.; Jeon, Eun-Seok; Schubert, Friederike; Nakano, Takahiro; Falk, Malin; Daccach Marques, Vanessa; Kleyman, Inna; Cherninkova-Gopina, Sylvia; Taniwaki, Takayuki; Planté-Bordeneuve, Violaine; Fayerman, Raisy; Tada, Satoshi; Endo, Hironobu; Montala, Carles; Lebellec, Loic; Guglielmino, Valeria; del Mar Saniger Alba, Maria; Salhi, Hayet; Cardoso Berensztejn, Amanda; Falcao de Campos, Catarina; Rougeaux, Isabelle; Le, An; Ayache, Samar S.; Kato, Nagaaki; Zwijack, Brittany; Gentile, Luca; Lindqvist, Per; Kuzume, Daisuke; Judge, Daniel P.; Sabatelli, Mario; Grapperon, Aude-Marie; Ueda, Mitsuharu; Fonder, Amie; Al-Salameh, Abdallah; Lecoq, Anne-Lise; Blasco Pelicano, Josep Miquel; Sirin Inan, Nermin G.; Labeyrie, Celine; Gragera Martínez, Álvaro; Imai, Akira; Brueckner, Caitlin; Su, Jen-Jen; Gilmore, Catherine; Meyrath, David; Gendre, Thierry; Hineno, Akiyo; Chahine, Ilonah; Boubrit, Yasmine; Kodaira, Minori; Yoshinaga, Tsuneaki; Shije, Jeffrey; Slama, Michel S.; Sekijima, Yoshiki; Rivera de la Parra, David; Nagai, Masahiro; Neves, Carlos; Moscardini, Mariana; Park, Jae Hong; Horga, Alejandro; Choumert, Ariane; Lim, He Eng Li; Valdrez, Katia; Miyahara, Teruyoshi; Wade, N. Kevin; Kim, Hee Jin; Thai, Desmond; de Azevedo Coutinho, Conceição; Bauer, Ralf; Ramalho, Joana; May, John; Joslin, Benjamin C.; Santos, Miguel Oliveira; Freimer, Miriam; Ulane, Christina; Megelin, Thomas; Pedrosa, Salve; Pilebro, Bjorn; Borrachero, Cristina; Sanz, Monica; Owusu-Sekyere, Mercy; Nguyen, Tyler; Echaniz-Laguna, Andoni; Altinkurt, Emre; Rodrigues, Leonardo; Zeldenrust, Steven R; Tsai, Li-Kai; Kabar, Iyad; Hamaguchi, Hirotoshi; Jiménez López, Brenda Poled; Green, Sinikka; Vorona, Elena; Waddington-Cruz, Márcia; Merlini, Giampaolo; Durmus, Hacer; Neshige, Shuichiro; Meyle, Eva; Goh, Khean Jin; Sahin, Erdi; Kleinschmidt, Natalia; Focseneanu, Cecile; Parman, Yesim; Rousseau, Antoine; Mekhael, Linda | article |  |
